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Showing 1–20 of 33 trials
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Published and searchable clinical trials
Evaluate Long-term Safety, Tolerability and Efficacy of Iptacopan in Study Participants With aHUS
NCT05795140
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +18 more
- Locations
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- Novartis Investigative Site São Paulo, Brazil
- Novartis Investigative Site Rio de Janeiro, Brazil
- Novartis Investigative Site Beijing, China
- Novartis Investigative Site Ostrava, Poruba, Czechia
NCT05935215
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +14 more
- Locations
-
- Novartis Investigative Site Nanjing, Jiangsu, China
- Novartis Investigative Site Beijing, China
- Novartis Investigative Site Beijing, China
- Novartis Investigative Site Shanghai, China
NCT07308574
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Research Site Bunkyō City, Japan
- Research Site Hirakata-shi, Japan
- Research Site Iruma-Gun, Japan
- Research Site Kyoto, Japan
NCT06312644
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +44 more
- Locations
-
- Research Site Boston, Massachusetts, United States
- Research Site Melbourne, Victoria, Australia
- Research Site Paris, France
- Research Site Essen, Norte-Westfalia, Germany
Developing a Pipeline to Employ RNA-Seq as a Complementary Diagnostic Tool in Rare Diseases
NCT05996731
- Conditions
- Abnormalities, Multiple, Anemia, Anemia, Hemolytic, +29 more
- Locations
-
- Centro di Ricerche Cliniche per le Malattie Rare "Aldo e Cele Daccò" Ranica, BG, Italy
NCT04745195
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Maastricht University Medical Center Maastricht, Limburg, Netherlands
Functional Implications of Rare Gene Mutations in aHUS Open the Door to Personalized Therapy
NCT05805202
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +14 more
- Locations
-
- Centro di Ricerche Cliniche per le Malattie Rare "Aldo e Cele Daccò" Ranica, BG, Italy
NCT01522183
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Clinical Trial Site Aurora, Colorado, United States
- Clinical Trial Site Washington D.C., District of Columbia, United States
- Clinical Trial Site Gainesville, Florida, United States
- Clinical Trial Site Atlanta, Georgia, United States
Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford
NCT01793168
- Conditions
- 1p36 Deletion Syndrome, 3-Methylglutaconic Aciduria, Type V, 4p Deletion Syndrome, Non-Wolf-Hirschhorn Syndrome, +698 more
- Locations
-
- Sanford Health Sioux Falls, South Dakota, United States
- Online Patient Enrollment System Sydney, Australia
NCT05726916
- Conditions
- Acute Kidney Injury, Anemia, Anemia, Hemolytic, +27 more
- Locations
-
- Tenon Hospital Paris, France
National Registry of Rare Kidney Diseases
NCT06065852
- Conditions
- AH Amyloidosis, AHL Amyloidosis, AL Amyloidosis, +207 more
- Locations
-
- Zoe Plummer Bristol, South West, United Kingdom
Study of NM8074 in Patients With aHUS With Evidence of Ongoing Thrombotic Microangiopathy
NCT05684159
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
Not specified
NCT04889430
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +14 more
- Locations
-
- USC Norris Cancer Center Los Angeles, California, United States
- Univ of California at Los Angeles Los Angeles, California, United States
- Univ Cali Irvine ALS Neuromuscular Orange, California, United States
- Univ of California at Sacramento Sacramento, California, United States
NCT04859608
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- CHU Amiens Picardie Amiens, France
- CHU d'Angers Angers, France
- Hôpital Tenon APHP Tenon, France
- CHU Besançon Besançon, France
NCT02222545
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +14 more
- Locations
-
- Omeros Investigational Site Duarte, California, United States
- Omeros Investigational Site Rochester, Minnesota, United States
- Omeros Investigational Site New York, United States
- Omeros Investigational Site Durham, North Carolina, United States
Study of Ravulizumab in Children and Adolescents With Atypical Hemolytic Uremic Syndrome (aHUS)
NCT03131219
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Research Site Hollywood, Florida, United States
- Research Site Atlanta, Georgia, United States
- Research Site Detroit, Michigan, United States
- Research Site Omaha, Nebraska, United States
NCT02949128
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Clinical Trial Site Fort Wayne, Indiana, United States
- Clinical Trial Site Fort Wayne, Indiana, United States
- Clinical Trial Site Durham, North Carolina, United States
- Clinical Trial Site Winston-Salem, North Carolina, United States
NCT03518203
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +19 more
- Locations
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- Children's Hospital Los Angeles (CHLA) Los Angeles, California, United States
- Cincinnati Children's Hospital Medical Center Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia (CHOP) Philadelphia, Pennsylvania, United States
NCT06004947
- Conditions
- Anemia, Anemia, Hemolytic, Anti-Neutrophil Cytoplasmic Antibody-Associated Vasculitis, +28 more
- Locations
-
- Celerion Tempe, Arizona, United States
NCT01770951
- Conditions
- Anemia, Anemia, Hemolytic, Atypical Hemolytic Uremic Syndrome, +15 more
- Locations
-
- Dunwoody, Georgia, United States
- Chicago, Illinois, United States
- Portland, Maine, United States
- Boston, Massachusetts, United States