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NCT05734196
- Conditions
- ATP-Binding Cassette Subfamily C Member 6 Deficiency, Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets, +18 more
- Locations
-
- Rady Children's Hospital San Diego, California, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Nationwide Children's Hospital Columbus, Ohio, United States
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Recruiting
PROPEL - A Prospective Observational Patient Registry to Evaluate ENPP1 and ABCC6 Deficiency
NCT06302439
- Conditions
- ATP-Binding Cassette Subfamily C Member 6 Deficiency, Arterial calcification of infancy, Ectonucleotide Pyrophosphatase/Phosphodiesterase 1 Deficiency
- Locations
-
- Ann and Robert H. Lurie Children's Hospital Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Mayo Clinic Rochester, Minnesota, United States
- CLINILABS Drug Development Corp Eatontown, New Jersey, United States
NCT06462547
- Conditions
- Arterial Calcification, Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets Type 2, +17 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
- Clinilabs Drug Development Corporation Eatontown, New Jersey, United States
- Necker-Enfants Malades Hospital Paris, France
- Universitätsklinikum Hamburg-Eppendorf (UKE) Hamburg, Germany
NCT03478839
- Conditions
- Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets Type2, Cardiovascular Diseases, +16 more
- Locations
-
- National Institutes of Health Clinical Center Bethesda, Maryland, United States
NCT05050669
- Conditions
- Adenosine Triphosphate Binding Cassette Transporter Protein Subfamily C Member 6, Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets, +3 more
- Locations
-
- Boston Children's Hospital Boston, Massachusetts, United States
- CHOP - Roberts Center for Pediatric Research Philadelphia, Pennsylvania, United States
- Cook Children's Hospital Fort Worth, Texas, United States
- CHU Sainte-Justine Montreal, Quebec, Canada
NCT05030831
- Conditions
- ATP-Binding Cassette Subfamily C Member 6 Deficiency, Arterial calcification of infancy, Cardiovascular Diseases, +15 more
- Locations
-
- Clinilabs Eatontown, New Jersey, United States
- Richmond Pharmacology Ltd (RPL) London, United Kingdom
Completed
Evaluation of Safety, Tolerability, and Efficacy of INZ-701 in Adults With ENPP1 Deficiency
NCT04686175
- Conditions
- Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets, Ectonucleotide Pyrophosphatase/Phosphodiesterase1 Deficiency, +2 more
- Locations
-
- Mayo Clinic Rochester, Minnesota, United States
- Clinilabs Drug Development Corporation Eatontown, New Jersey, United States
- University of Saskatchewan Saskatoon, Saskatchewan, Canada
- Necker University Hospital-Sick Children Paris, France
NCT04372446
- Conditions
- Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets Type 2, Generalized Arterial Calcification in Infancy
- Locations
-
- Engage Health Eagan, Minnesota, United States
Active, Not Recruiting
The ENERGY 3 Study: Evaluation of Efficacy and Safety of INZ-701 in Children With ENPP1 Deficiency
NCT06046820
- Conditions
- Arterial calcification of infancy, Autosomal Recessive Hypophosphatemic Rickets, Ectonucleotide Pyrophosphatase/Phosphodiesterase1 Deficiency, +2 more
- Locations
-
- Children's Hospital of Colorado Aurora, Colorado, United States
- Ann & Robert H. Lurie Children's Hospital Chicago, Illinois, United States
- Boston Children's Hospital Boston, Massachusetts, United States
- Nationwide Children's Hospital Columbus, Ohio, United States