Completed Baby Detect : Genomic Newborn Screening NCT05687474 Conditions 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more Locations CRMN, Hôpital La Citadelle — Liège, Wallonia, Belgium View Trial Details
Completed Newborn Screening for Aromatic L-amino Acid Decarboxylase Deficiency NCT02399761 Conditions Aromatic L-amino Acid Decarboxylase Deficiency, Aromatic amino acid decarboxylase deficiency Locations National Taiwan University Hospital — Taipei, Taiwan View Trial Details
Active, Not Recruiting A Trial to Evaluate Safety and Efficacy of a Product Named VGN-R09b in Severe AADC Deficiency NCT06432140 Conditions Aromatic L-amino Acid Decarboxylase Deficiency, Aromatic amino acid decarboxylase deficiency Locations Shanghai — Shanghai, Shanghai Municipality, China View Trial Details