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Published and searchable clinical trials
NCT06512454
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- University of Florida Gainesville, Florida, United States
- University of South Carolina Charleston, South Carolina, United States
- Vanderbilt University Medical Center Nashville, Tennessee, United States
- Vienna General Hospital (AKH Wien) Vienna, Austria
NCT05677971
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- St. Joseph's Hospital and Medical Center Phoenix, Arizona, United States
- Mayo Clinic Phoenix, Arizona, United States
- University of Arizona Thomas D. Boyer Liver Institute Tucson, Arizona, United States
NCT06165341
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- St Joseph's Hospital and Medical Center Phoenix, Arizona, United States
- Mayo Clinic - PPDS Phoenix, Arizona, United States
- University of Arizona Thomas D. Boyer Liver Institute Tucson, Arizona, United States
- University of California San Diego La Jolla, California, United States
Preparation of IPSC for Cell Gene Editing for the Treatment of AATD
NCT06892236
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
-
- Fondazione IRCCS Policlinico San Matteo, Sc Pneumologia Pavia, Italy
NCT04722887
- Conditions
- Alpha1-Antitrypsin Deficiency, Chronic Disease, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +14 more
- Locations
-
- UCLA Medical Center Los Angeles, California, United States
- University of Florida Gainesville, Florida, United States
- University of Miami Miami, Florida, United States
- Cleveland Clinic Cleveland, Ohio, United States
NCT04474197
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- University of Alabama at Birmingham Birmingham, Alabama, United States
- David Geffen School of Medicine at UCLA Los Angeles, California, United States
- University of California Davis Medical Center Sacramento, California, United States
- National Jewish Health Denver, Colorado, United States
NCT02870348
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- Hiroskai University Hospital Aomori, Japan
- Hokkaido University Hospital Hokkaido, Japan
- Juntendo University Hospital Tokyo, Japan
NCT02870309
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
-
- Hokkaido University Hospital Sapporo, Japan
- Juntendo University Hospital Tokyo, Japan
NCT02525861
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
-
- Arizona Board of Regents, University of Arizona Tucson, Arizona, United States
- UCLA Medical Center Los Angeles, California, United States
- Cedars Sinai Medical Center, Division of Pulmonary and Critical Care Medicine Los Angeles, California, United States
- University of California Davis Health System Sacramento, California, United States
GLASSIA Infusion Rate Study
NCT01651351
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +11 more
- Locations
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- Overland Park, Kansas, United States
NCT00157092
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- Shands Hospital at the University of Florida Gainesville, Florida, United States
NCT00161707
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- National Jewish Medical and Research Center Denver, Colorado, United States
- Shands Hospital at the University of Florida Gainesville, Florida, United States
- Cleveland Clinic Foundation, Department of Pulmonary and Critical Care Medicine Cleveland, Ohio, United States
- The University of Texas Health Science Center at Tyler Tyler, Texas, United States
An Extension Study to Learn About the Long-Term Safety of Fazirsiran and if Fazirsiran Can Help People With Alpha-1 Antitrypsin Liver Disease
NCT05899673
- Conditions
- Alpha1-Antitrypsin Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +9 more
- Locations
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- UCSD Altman Clinical and Translational Research Institute La Jolla, California, United States
- Stanford Medicine Outpatient Center Redwood City, California, United States
- UF Clinical and Translational Science Institute Gainesville, Florida, United States
- University Of Iowa Hospitals And Clinics Iowa City, Iowa, United States