Recruiting Longitudinal Natural History Study of Patients With Peroxisome Biogenesis Disorders (PBD) NCT01668186 Conditions ACBD5 (AcylCoA Binding Domain 5) Deficiency, ATP Binding Cassette Subfamily D Member 3 Gene Mutation, Abnormalities, Multiple, +48 more Locations Research Institute of the McGill University Health Center — Montreal, Quebec, Canada View Trial Details
Active, Not Recruiting MT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis NCT02171104 Conditions Abnormalities, Multiple, Acyl-CoA Oxidase Deficiency, Adrenoleukodystrophy With Cerebral Involvement, +85 more Locations Masonic Cancer Center, University of Minnesota — Minneapolis, Minnesota, United States View Trial Details