Completed Longitudinal Studies of the Glycoproteinoses NCT01891422 Conditions Alpha Mannosidosis, Aspartylglucosaminuria, Beta Mannosidosis, +29 more Locations Greenwood Genetic Center — North Charleston, South Carolina, United States View Trial Details
Completed Safety Study of Recombinant Human Alpha-mannosidase for the Treatment of Patients With Alpha-mannosidosis NCT01268358 Conditions Alpha Mannosidosis, Carbohydrate Metabolism, Inborn Errors, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +7 more Locations Not specified View Trial Details
Completed The Natural History of Alpha-Mannosidosis NCT00498420 Conditions Alpha Mannosidosis, Bone Diseases, Bone Diseases, Developmental, +15 more Locations Department of Pediatrics, Charles University — Prague, Czechia University of Mainz — Mainz, Germany Department of Medicine, University of Tromsoe — Tromsø, Norway Willink Biochemical Genetics Unit,. Royal Manchester Children's Hospital — Manchester, United Kingdom View Trial Details
Completed Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders NCT01043640 Conditions Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +52 more Locations Masonic Cancer Center, University of Minnesota — Minneapolis, Minnesota, United States View Trial Details