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Published and searchable clinical trials
Adrenoleukodystrophy National Registry Study
NCT03789721
- Conditions
- ALD (Adrenoleukodystrophy), Adrenal Gland Diseases, Adrenal Insufficiency, +23 more
- Locations
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- Masonic Cancer Center at University of Minnesota Minneapolis, Minnesota, United States
NCT04528355
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +119 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
NCT01962415
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +125 more
- Locations
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- UPMC Children's Hospital of Pittsburgh Pittsburgh, Pennsylvania, United States
The Myelin Disorders Biorepository Project
NCT03047369
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
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- Children's Hospital of Los Angeles Los Angeles, California, United States
- Children's Hospital of Orange County Orange, California, United States
- Stanford University (Lucile Packard Children's Hospital) Palo Alto, California, United States
- University of California, Davis (UC Davis Health) Sacramento, California, United States
NCT04925349
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +37 more
- Locations
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- AP-HP Hôpital Bicêtre Le Kremlin-Bicêtre, France
- AP-HP Hôpital La Pitié Salpêtrière Paris, France
IT and IV Lentiviral Gene Therapy for X-ALD
NCT03727555
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Shenzhen Geno-immune Medical Institute Shenzhen, Guangdong, China
NCT02254863
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +55 more
- Locations
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- Duke University Medical Center Durham, North Carolina, United States
NCT06224413
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States
- Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
- UT Southwestern Medical Center Dallas, Texas, United States
NCT05443906
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +33 more
- Locations
-
- Kennedy Krieger Institute Baltimore, Maryland, United States
NCT06796920
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +26 more
- Locations
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- Beijing TianTan Hospital Beijing, Beijing Municipality, China
- The 958 Hospital of Chinese People's Liberation Army, The Jiangbei Campus of Southwest Hospital, The First Affiliated Hospital of Army Medical University Chongqing, Chongqing Municipality, China
- the Southwest hospital Chongqing, Chongqing Municipality, China
- Jingmen No.1 People's Hospital Jingmen, Hubei, China
NCT04675749
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Leipzig University Medical Center, Leukodystrophy Outpatient Clinic, Department of Neurology, Leipzig, Germany Leipzig, Saxony, Germany
Longitudinal Study of Ultra-rare Inherited Metabolic and Degenerative Neurological Diseases.
NCT04880356
- Conditions
- 2-Hydroxyglutaricaciduria, Adrenal Gland Diseases, Adrenal Insufficiency, +58 more
- Locations
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- Fondazione IRCCS Istituto Neurologico Carlo Besta Milan, Milano, Italy
NCT06178120
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Paris Brain Institute (ICM) Centre Hospitalier Universitaire Pitié Salpêtrière Paris, France
Registry of X-linked Adrenoleukodystrophy
NCT05939232
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Beijing Tiantan Hospital Beijing, China
Validation of a Prognostic Biomarker Using Brain Diffusion MRI in X-linked Adrenoleukodystrophy
NCT05911919
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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Not specified
NCT02699190
- Conditions
- 4H Syndrome, ADLD, AGS, +173 more
- Locations
-
- The Children's Hospital of Philadelphia Philadelphia, Pennsylvania, United States
Baby Detect : Genomic Newborn Screening
NCT05687474
- Conditions
- 3-Hydroxy 3-Methyl Glutaric Aciduria, 3-Hydroxy-3-Methylglutaryl-CoA Lyase Deficiency, 3-Hydroxy-3-Methylglutaryl-CoA Synthase 2 Deficiency, +368 more
- Locations
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- CRMN, Hôpital La Citadelle Liège, Wallonia, Belgium
A Clinical Study to Evaluate the Efficacy and Safety of MIN-102 (IMP) in Male AMN Patients.
NCT03231878
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +21 more
- Locations
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- Stanford University Medical Center Stanford, California, United States
- Kennedy Krieger Institute Baltimore, Maryland, United States
- Massachusetts General Hospital Boston, Massachusetts, United States
- Hospital de la Pitié-Salpêtrière Paris, France
NCT03852498
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
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- Lucile Packard Children's Hospital Palo Alto, California, United States
- Boston Children's Hospital/Massachusetts General Hospital Boston, Massachusetts, United States
- University of Minnesota Minneapolis, Minnesota, United States
- Hôpital Robert Debré Paris, France
NCT04687007
- Conditions
- Adrenal Gland Diseases, Adrenal Insufficiency, Adrenoleukodystrophy, +22 more
- Locations
-
- Leipzig University Medical Center, Leukodystrophy Outpatient Clinic, Department of Neurology, Leipzig, Germany Leipzig, Saxony, Germany
- Leukodystrophy Outpatient Clinic Leipzig, Germany