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An Observational LTFU Study for Patients Previously Treated With Autologous ex Vivo Gene Therapy for ADA-SCID
NCT04049084
- Conditions
- Adenosine Deaminase Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, DNA Repair-Deficiency Disorders, +10 more
- Locations
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- Mattel Children's Hospital UCLA/Ronald Reagan UCLA Medical Center Los Angeles, California, United States
- UCL Great Ormond Street Institute of Child Health London, United Kingdom
Completed
EZN-2279 in Patients With ADA-SCID
NCT01420627
- Conditions
- ADA-SCID, Adenosine Deaminase Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
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- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California San Francisco San Francisco, California, United States
- National Jewish Health Denver, Colorado, United States
- UBMD Buffalo, New York, United States
NCT00008450
- Conditions
- Adenosine Deaminase Deficiency, Autosomal Recessive Disorder, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +17 more
- Locations
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- Fred Hutch/University of Washington Cancer Consortium Seattle, Washington, United States
NCT02022696
- Conditions
- ADA-SCID, Adenosine Deaminase Deficiency, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
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- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States