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NCT03338816
- Conditions
- ALA Dehydratase Deficient Porphyria (ADP), Acute Hepatic Porphyria, Acute Intermittent Porphyria, +17 more
- Locations
-
- Clinical Trial Site Little Rock, Arkansas, United States
- Clinical Trial Site San Francisco, California, United States
- Clinical Trial Site Boston, Massachusetts, United States
- Clinical Trial Site Ann Arbor, Michigan, United States
NCT02949830
- Conditions
- Acute Intermittent Porphyria, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +10 more
- Locations
-
- Clinical Trial Site San Francisco, California, United States
- Clinical Trial Site New York, United States
- Clinical Trial Site Galveston, Texas, United States
- Clinical Trial Site Stockholm, Sweden
Completed
A Phase 1 Study of Givosiran (ALN-AS1) in Patients With Acute Intermittent Porphyria (AIP)
NCT02452372
- Conditions
- Acute Intermittent Porphyria, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +10 more
- Locations
-
- Clinical Trial Site Birmingham, Alabama, United States
- Clinical Trial Site San Francisco, California, United States
- Clinical Trial Site New York, United States
- Clinical Trial Site Galveston, Texas, United States
NCT00418795
- Conditions
- Acute Intermittent Porphyria, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Digestive System Diseases, +10 more
- Locations
-
- Univercity Texas Medical Branch Galveston, Texas, United States
Active, Not Recruiting
Acute Porphyria Biomarkers for Disease Activity
NCT02935400
- Conditions
- Acute Intermittent Porphyria, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, Coproporphyria, Hereditary, +14 more
- Locations
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- University of Texas Medical Branch Galveston, Texas, United States