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Treatment Frequency Reduction in Pompe Disease
NCT06575829
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
-
Not specified
NCT03893240
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
-
- Barrow Neurological Institute Phoenix, Arizona, United States
- University of California Irvine Health Orange, California, United States
- University of Kansas Medical Center Kansas City, Kansas, United States
- University of Minnesota Medical School Minneapolis, Minnesota, United States
Completed
Safety and Efficacy Evaluation of Repeat neoGAA Dosing in Late Onset Pompe Disease Patients.
NCT01898364
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +15 more
- Locations
-
- Investigational Site Number 840006 Phoenix, Arizona, United States
- Investigational Site Number 840010 Jacksonville, Florida, United States
- Investigational Site Number 840001 Kansas City, Kansas, United States
- Investigational Site Number 840008 St Louis, Missouri, United States
Active, Not Recruiting
A Gene Transfer Study for Late-Onset Pompe Disease (RESOLUTE)
NCT04093349
- Conditions
- Acid Maltase Deficiency, Brain Diseases, Brain Diseases, Metabolic, +17 more
- Locations
-
- Barrow Neurological Institute Phoenix, Arizona, United States
- University of California Irvine Health Orange, California, United States
- Emory University School of Medicine Atlanta, Georgia, United States
- University of Kansas Medical Center Research Institute Kansas City, Kansas, United States