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Safety and Efficacy of AAV9/AP4B1 (BFB-101) For Patients With AP4B1-related Hereditary Spastic Paraplegia Type 47 (SPG47)
NCT06948019
- Conditions
- AP4B1, Central Nervous System Diseases, Congenital Abnormalities, +31 more
- Locations
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- Boston Children's Hospital Boston, Massachusetts, United States