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NCT01852071
- Conditions
- ADA-SCID, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
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- Mattel Children's Hospital, UCLA Los Angeles, California, United States
- Mark O. Hatfield Clinical Research Center, NIH Bethesda, Maryland, United States
Completed
EZN-2279 in Patients With ADA-SCID
NCT01420627
- Conditions
- ADA-SCID, Adenosine Deaminase Deficiency, Congenital, Hereditary, and Neonatal Diseases and Abnormalities, +10 more
- Locations
-
- Children's Hospital Los Angeles Los Angeles, California, United States
- University of California San Francisco San Francisco, California, United States
- National Jewish Health Denver, Colorado, United States
- UBMD Buffalo, New York, United States
NCT02022696
- Conditions
- ADA-SCID, Adenosine Deaminase Deficiency, Severe combined immunodeficiency due to adenosine deaminase deficiency
- Locations
-
- National Institutes of Health Clinical Center, 9000 Rockville Pike Bethesda, Maryland, United States